EIN: 88-1577647 · Glendale, CA
Cure ADSSL1 is a patient-led non-profit organization founded by parents Priyanka and Naveen, whose children were diagnosed with the rare neuromuscular disease ADSS(L)1 Myopathy. This organization emerged from their personal journey of navigating the challenges of this ultra-rare condition, caused by a mutation in the ADSS(L)1 gene. By partnering with researchers and organizations, they are committed to driving efforts towards developing a treatment.
Cure ADSSL1 aims to develop a treatment for ADSS(L)1 Myopathy through collaboration with leading researchers. The focus is on gene therapy, with the hope of improving the quality of life for affected individuals and their families.
Donations to Cure ADSSL1 directly support critical research efforts to find a cure for ADSS(L)1 Myopathy, a disease affecting fewer than 200 individuals worldwide. Every contribution, no matter how small, plays a crucial role in advancing research and providing hope for families facing this devastating condition.
Your support can make a difference! Donate cryptocurrency or cash today to help fund groundbreaking research and bring hope to families affected by ADSS(L)1 Myopathy. Together, we can find a cure!
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